Spark Therapeutics, Inc., based in Philadelphia, PA, is a pioneering gene therapy company dedicated to transforming healthcare through innovative genetic treatments. With a focus on inherited diseases such as inherited retinal diseases, hemophilia, and neurodegenerative disorders, Spark combines cutting-edge vector design, advanced manufacturing capabilities, and a strong commitment to improving patient care. Through their fully integrated approach, Spark Therapeutics aims to unlock the potential of gene therapy to create groundbreaking medicines that address unmet medical needs. Their mission is to lead the way in gene therapy innovation, driving healthcare transformation and sparking change in the local community through collaboration and excellence in research, development, and commercial operations.Generated from the website