Rocket Pharmaceuticals, Inc. is a biotech company based in Cranbury, NJ, specializing in the development of curative gene therapies for patients with complex and rare life-threatening disorders. With a mission to seek gene therapy cures, Rocket Pharma aims to correct the root cause of these devastating diseases through their integrated pipeline of genetic therapies.
Driven by their core values of trust, generosity, curiosity, and elevation, Rocket Pharmaceuticals is dedicated to putting patients and their families first. Their team of experienced leaders in the biotech industry has enabled them to rapidly advance their programs, moving four of them into the clinic within just two years. Through their strategic approach to gene therapy, Rocket Pharma is focused on directly targeting the genetic mutation in affected cells for various rare disorders, including Fanconi Anemia, Leukocyte Adhesion Deficiency-I, Danon Disease, Pyruvate Kinase Deficiency, and more.
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